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Introduction to muscular dystrophy / Raymond A. Huml
Muscular dystrophy : historical background and types / Raymond A. Huml
FSHD : the most common type of muscular dystrophy? / Raymond A. Huml and Daniel P. Perez
Duchenne and Becker muscular dystrophies : underlying genetic and molecular mechanisms / Jean K. Mah
An overview of the other muscular dystrophies : underlying genetic and molecular mechanisms / Jean K. Mah
Transition from childhood to adult in patients with muscular dystrophy / Elba Yesi Gerena Maldonado and Kathryn R. Wagner
Overview of current treatments for muscular dystrophy / Zheng (Jane) Fan
Physical therapy and orthotic devices / Laura E. Case
Orthopedic management of the child with muscular dystrophy / Robert K. Lark and Elizabeth W. Hubbard
Global regulatory landscape / Raymond A. Huml
Key challenges to the approval of products to treat patients with muscular dystrophy / Raymond A. Huml
Pharmaceutical products and non-pharmaceutical interventions as potential treatments for patients with muscular dystrophy / Raymond A. Huml
US patient advocacy groups / Meredith L. Huml
Global and national patient registries / Raymond A. Huml
Summary / Raymond A. Huml.
Muscular dystrophy : historical background and types / Raymond A. Huml
FSHD : the most common type of muscular dystrophy? / Raymond A. Huml and Daniel P. Perez
Duchenne and Becker muscular dystrophies : underlying genetic and molecular mechanisms / Jean K. Mah
An overview of the other muscular dystrophies : underlying genetic and molecular mechanisms / Jean K. Mah
Transition from childhood to adult in patients with muscular dystrophy / Elba Yesi Gerena Maldonado and Kathryn R. Wagner
Overview of current treatments for muscular dystrophy / Zheng (Jane) Fan
Physical therapy and orthotic devices / Laura E. Case
Orthopedic management of the child with muscular dystrophy / Robert K. Lark and Elizabeth W. Hubbard
Global regulatory landscape / Raymond A. Huml
Key challenges to the approval of products to treat patients with muscular dystrophy / Raymond A. Huml
Pharmaceutical products and non-pharmaceutical interventions as potential treatments for patients with muscular dystrophy / Raymond A. Huml
US patient advocacy groups / Meredith L. Huml
Global and national patient registries / Raymond A. Huml
Summary / Raymond A. Huml.